Supporting national policy making – “Extending the availability of drugs to combat Alzheimer’s disease”
Submitting Institution
University of ExeterUnit of Assessment
Public Health, Health Services and Primary CareSummary Impact Type
HealthResearch Subject Area(s)
Medical and Health Sciences: Public Health and Health Services
Summary of the impact
About 800,000 people are living with Alzheimer's disease in the UK today,
at a cost of about £23
Billion/annum. Researchers in Exeter produced a report in 2010 about the
effectiveness and cost-
effectiveness of available drugs, which formed the basis for revised NICE
guidelines (2011),
recommending more widespread drug usage. 2012 NHS data showed a big
increase in drug
prescribing since 2010. We estimate that if the 110,000 people with
untreated mild disease at the
time of the report are now being treated, there would be an average delay
in time to admission to
care of 13,000 person years.
Underpinning research
In 2010, as part of its contract to support NICE, the University of
Exeter's Peninsula Technology
Group (PenTAG), led by Professor Hyde (appointed 2009) produced a health
technology
assessment (HTA) about the treatment of Alzheimer's disease with
anticholinesterase (AChE)
inhibitors. This HTA considered new evidence on the effectiveness and
cost-effectiveness of
donepezil, rivastigmine, galantamine and memantine in the treatment of
Alzheimer's disease,
superseding the 2004 HTA report that had informed the previous NICE
guidance. Although not
formally published in the HTA Monograph series until 2012 (Bond et al)1,
the report was completed
in June 2010 and considered by the Appraisal Committee of NICE in August
2010, who then
issued their new guidance in March 2011. The report by PenTAG included
systematic reviews,
meta-analyses and mixed treatment comparisons of RCTs (both the new
evidence alone and
cumulatively with previous evidence), systematic reviews of
cost-effectiveness evaluations, critical
appraisals of three manufacturer submissions and a new cost-effectiveness
model, subsequently
published in peer review journals (Hyde et al, Peters et al) 2,3.
The findings showed a consolidation
of evidence on the effectiveness of donepezil, rivastigmine, galantamine
and slightly enhanced
evidence on the effectiveness of memantine. For instance a statistically
significant beneficial effect
on measures of patient function and global impact emerged when randomised
controlled trials
comparing memantine with best-supportive care were formally meta-analysed
in our report. This
was not apparent previously. The most marked change was on the evidence on
cost-effectiveness,
which was greatly improved for donepezil, rivastigmine and galantamine and
slightly improved for
memantine relative to the assessment in 2004. The PenTAG model
demonstrated that each of the
AChE inhibitors was cost saving compared with best supportive care, and
that for memantine the
incremental cost-effectiveness ratio was £32,100/QALY gained. As well as
including cutting edge
analytical methods the report also included novel methods of presenting
large volumes of research
data of a complex nature (Pitt et al)4.
Each piece of NICE guidance in the technology appraisal programme is
supported by an
independent academic report. In the multiple technology appraisal process
a health technology
assessment (HTA), generally comprising systematic reviews, meta-analyses
and health economic
modelling, is prepared by an academic group. The Exeter based Peninsula
Technology
Assessment Group (PenTAG) has been performing this role for 12 years and
has conducted over
30 HTAs, all published in peer reviewed journals. The work is funded by DH
through the NIHR HTA
Programme. This is currently in its fourth period of renewal, which will
run until 2016. The work was
led by Professor Ken Stein until 2009 and subsequently by Professor Chris
Hyde. The PenTAG
group working on the Alzheimer's drug appraisal, while led by Hyde, was
multidisciplinary,
including economists (Anderson and Hoyle) as well as experts in systematic
reviews (Hyde, Bond,
Peters and others), and used new methodological approaches developed
within the group (Pitt et
al 2009)4.
Grant:
Stein K. Technology Appraisal Reports (TARs). Dept of Health. April 2005
to March 2011.
£2,430,000
References to the research
Evidence of the quality of the research is clear from the following four
publications in high quality
peer-review journals:
1. Bond M, Rogers G, Peters J, Anderson R, Hoyle M, Miners A, Moxham T,
Davis S, Thokala
P, Wailoo A, Jeffreys M, Hyde, C.. The effectiveness and
cost-effectiveness of donepezil,
galantamine, rivastigmine and memantine for the treatment of Alzheimer's
disease (review
of NICE technology appraisal guidance 111): a systematic review and
economic model.
Health Technol Assess 2012;16(21):1-470.
2. Hyde C, Peters J, Bond M, Rogers G, Hoyle M, Anderson R, Jeffreys M,
Davis S, Thokala
P, Moxham T. Evolution of the evidence on the effectiveness and
cost-effectiveness of
acetylcholinesterase inhibitors and memantine for Alzheimer's disease:
systematic review
and economic model. Age and Ageing 2013;42(1):14-20.
3. Peters J, Anderson R, Hoyle M, Hyde C. Evolution of a cost utility
model of donepezil for
Alzheimer's disease. Int J Technol Assess Health Care
2013;29:147-154.
doi:10.1017/S026646231300007X.
4. Pitt M, Stahl-Timmins W, Anderson R, Stein K. Using information
graphics in health
technology assessment. Toward a structured approach. Int J Technol
Assess Heath Care
2009;25(4):555-563. DOI: 10.1017/S0266462309990286
Details of the impact
The NICE appraisal process depends on evaluations of efficacy and
cost-effectiveness in various
circumstances, and these appraisals are always based in the multiple
technology appraisal
process on the work of independent academic centres such as PenTAG 1,2.
The reports are HTAs
which generally consist of systematic reviews, meta-analyses and health
economic models
combined. The impact NICE has made since its inauguration is acknowledged
to be partly
attributable to the high quality of the independent academic reports
delivered in tight timescales.
NICE guidelines are now recognised to be of importance throughout the
developed world 3 The
Exeter based PenTAG group has contributed greatly to this process through
its many reports for
NICE and its methodological research.
The specific project (HTA 09/87/01) was commissioned by the NETSCC HTA
programme on
behalf of NICE in November 2009 with the title `The effectiveness and
cost-effectiveness of
donepezil, galantamine, rivastigmine and memantine for the treatment of
Alzheimer's disease
(Review of TA111)'. The project was to review and update the evidence
presented to NICE in 2004
of how good a number of drugs were for treating Alzheimer's disease. The
assessment would also
assess whether the reviewed drugs were likely to be considered good value
for money for the
NHS. The final technology appraisal report, consisting of systematic
reviews, meta-analyses and
mixed treatment comparisons of RCTs (both the new evidence alone and
cumulatively with
previous evidence), systematic reviews of cost-effectiveness evaluations,
critical appraisals of
three manufacturer submissions and a de novo cost-effectiveness model was
submitted in June
2010 and considered by the NICE Appraisal Committee in August 2010 3.
In the previous guidance NICE in 2004 had recommended that donepezil,
galantamine and
rivastigmine could be used for people with moderate Alzheimer's disease
but memantine could
only be used in clinical trials.
The report from PenTAG 4was the key piece of evidence that
informed the decision by NICE's
Appraisal Committee to provide its 2011 guidance, which extended the
availability of donepezil,
galantamine and rivastigmine to people with mild Alzheimer's disease, and
allowed memantine to
be used with those with severe forms of the disease for the first time5.
This guidance was released
in March 2011. It is mandatory for NHS commissioners to adhere to any
technology appraisal
guidance released. Data for prescribing in England published on the NHS
Health and Social Care
website indicates that there has been a massive increase in use of these
drugs between 2010, the
year before the 2011 NICE guidance was released, and 2012, the first
complete year after
(although arguably the full extent of the effect on prescribing may not be
seen until the 2013, the
data for which are not yet available). Between 2010 and 2012 donepezil use
increased by 41%,
rivastigmine by 51% and memantine by 278%, with 3% decrease in use of
galantamine6,7. Based
on the results of the economic model in our HTA we estimate that there
were 110,000 persons with
"untreated" mild Alzheimer's disease in England and Wales at the time of
the change in guidance
and if these individuals are now prescribed either donepezil or
galantamine or rivastigmine we can
expect on average cognition to be improved by 4% (absolute increase) in
this population and there
to be a cumulative delay in time to admission to long term care of 13,000
person/years. Similarly
we estimate that there were 103,000 persons with "untreated" severe
Alzheimer's disease in
England and Wales at the time of the change in guidance and if these
individuals are now
prescribed memantine we can expect on average cognition to be improved by
3% (absolute
increase) in this population and there to be a cumulative delay in time to
admission to long term
care of 8,000 person/years, with consequential large financial savings.
The change in decision about recommended drugs was directly attributed by
NICE to change in
the evidence, the key source of which was PenTAG's independent academic
report8,9,10. The NICE
decision on drugs for Alzheimer's disease thus provides a clear example of
how PenTAG's
research makes an impact on national policy making, and the important
influence of the
independent academic report is always reflected in the NICE appraisal
process. In addition, NICE
does have great worldwide influence3, so we expect that this
work has had beneficial impacts on
the treatment on patients with Alzheimer's disease throughout the world.
Sources to corroborate the impact
To support the central role of independent academic reports in the NICE
appraisal process:
-
1.
http://www.nice.org.uk/aboutnice/howwework/devnicetech/developing_nice_multiple_technology_appraisals.jsp
and
-
http://www.nice.org.uk/media/B52/A7/TAMethodsGuideUpdatedJune2008.pdf
To support the worldwide importance of NICE:
- http://www.nytimes.com/2008/12/03/health/03nice.html?pagewanted=all
PenTAG report to NICE:
- http://www.nice.org.uk/nicemedia/live/12248/49789/49789.pdf
NICE's guidance on drugs for Alzheimer's disease:
- http://www.nice.org.uk/guidance/index.jsp?action=byID&o=13419
To support changes in drug prescribing:
-
https://catalogue.ic.nhs.uk/publications/prescribing/primary/pres-cost-anal-eng-2012/pres-
cost-anal-eng-2012a-rep.pdf
and
- https://catalogue.ic.nhs.uk/publications/prescribing/primary/pres-cost-anal-eng-2010/pres-
cost-anal-eng-2010-rep.pdf
To support NICE attributing change in guidance to change in evidence:
-
http://www.bbc.co.uk/news/health-11486367
and
-
9.
http://www.telegraph.co.uk/health/healthnews/8045775/Alzheimers-u-turn-by-Nice-to-allow-drugs-for-mild-cases.html
and
- http://www.channel4.com/news/alzheimers-drug-u-turn-welcomed